World Orphan Drug Congress US

Thank you for speaking with the ICON team at World Orphan Drug Congress.

We understand the unique strategic, operational, medical and scientific challenges that rare disease clinical trials present, and we invite you to explore how we are leading the way in Rare Disease drug development.

Patient-Centered Trial Development Toolkit

Participant-focused tools designed to improve study success in rare disease clinical trials

Factsheet: Accellacare In-Home Services

Bringing the trial to the patient

Factsheet: Language Services

Full-service translation and clinical translation program management

Factsheet: Biotech

Developing transformative therapies requires a flexible approach

Case Study:

Trial decentralisation enhances clinical research accessibility and reduces burden on rare disease patient population

Case Study:

Overcoming operational challenges and exceeding recruitment timeline in an adult patient population with Fibrodysplasia Ossificans Progressiva

Whitepaper: DE&I in rare disease - Beyond buzzwords: Diversity, equity and inclusion in rare disease clinical trials

Explore barriers and effective strategies to mirroring the patient community make-up in rare disease clinical trials, challenges that rare disease PAOs are tackling to improve DE&I and the consequences of getting it ‘wrong’ in the clinical stage and beyond