ICON has experience in Orphan diseases

These include:

  • Wilson’s Disease
  • Transplant/Bone marrow
  • Anthracycline extravasation
  • Hyperoxaluria/Enteric, Crohn’s Disease
  • Pemphigus Vulgaris, Myasthenia Gravis
  • Atypical Hemolytic Uremic Syndrome (aHUS)
  • Cystic Fibrosis
  • Hereditary Angioedema (HAE)
  • Various Neurological Disorders